Dados do Trabalho
Título
PATISIRAN GLOBAL OPEN-LABEL EXTENSION STUDY AT 36 MONTHS: EFFECT OF LONG-TERM TREATMENT ON MORTALITY AND AMBULATORY FUNCTION IN PATIENTS WITH HATTR AMYLOIDOSIS WITH POLYNEUROPATHY
Palavras-chave
hATTR amyloidosis; polyneuropathy; patisiran; PAF
Área
Ensaios clínicos
Autores
Jonas Wixner, Mitsuharu Ueda, Wilson Marques Junior, Samir Dalia, Seth Arum, Cecilia Hale, Patrick Jay, Kelley Capocelli, David Adams