Dados do Trabalho
Título
NFL LEVELS SIGNIFICANTLY DECREASE IN RESPONSE TO TREATMENT WITH PATISIRAN OR VUTRISIRAN IN HATTR AMYLOIDOSIS WITH POLYNEUROPATHY
Palavras-chave
biomarker; monitoring; FAP
Área
Ensaios clínicos
Autores
Emre Aldinc, Simina Ticau, Raphael Sayegh, Michael Polydefkis, Hans Nienhuis, Chafic Karam, Senda Ajroud-Driss, Yoshiki Sekijima, Marcia Waddington-Cruz, Jennifer Barnes, Paul Nioi